The dystrophin gene has 79 exons. #ExonSkipping therapies aim to skip specific exons to help the body work around certain mutations. Genetic testing can identify which exons are affected and if this approach may apply.
Learn more: https://www.wespeakduchenne.com
#Duchenne #NSPharma https://x.com/NSPharmaInc/status/2038628623356244477/photo/1
We’re looking forward to this upcoming community event and the chance to engage in meaningful conversations around #RareDisease care.
Listening, learning and sharing perspectives helps move progress forward. We look forward to connecting!
Learn more: https://ow.ly/kJST50YzCCz https://x.com/NSPharmaInc/status/2037545713618300979/photo/1
When the immune system turns against the body, rare diseases like #EGPA can emerge.
Marked by asthma, rashes, and nerve pain, EGPA involves overactive eosinophils and inflammation.
NS-229, a JAK1 inhibitor, is now in a global Phase 2 trial.
Learn More: https://ow.ly/AUPf50YyAY3 https://x.com/NSPharmaInc/status/2036820476673052777/video/1
Duchenne is part of the story, not the whole story.
Brantley was diagnosed with DMD at 4. #ExonSkipping therapies can help produce a usable form of dystrophin, slowing progression so patients can keep pursuing what they love.
Learn more: https://ow.ly/tLgj50Yy39p https://x.com/NSPharmaInc/status/2036458150723768404/video/1
We’re proud to support the 2026 Brian McKenna #TetraSki Express National Championship on March 27 in Utah!
This inspiring event showcases adaptive technology, resilience and athleticism in downhill racing.
Learn more: http://www.tetraski.us/tetraski-express
#AdaptiveSports #NSPharma https://x.com/NSPharmaInc/status/2034993922947063856/photo/1
We’re glad to be part of this upcoming #CureDuchenne event!
These moments help us reflect, connect and stay focused on improving care and access. We look forward to seeing you there.
Learn more: https://web.cvent.com/event/a4ee9964-3748-4016-b032-1b4c3b2df2f0/summary
#NSPharma https://x.com/NSPharmaInc/status/2034284219602489364/photo/1
Thanks to #Project Alive and the #HunterSyndrome community for a meaningful Building a Future Together Conference!
It was inspiring to connect with families, advocates and leaders in Costa Mesa and share conversations that help advance rare disease care and research.
#NSPharma https://x.com/NSPharmaInc/status/2033559440838852717/photo/1
