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nspharmainc NS Pharma @nspharmainc ·
12 Nov

Leber congenital amaurosis is caused by mutations in the GUCY2D gene, disrupting retinal function.

We're partnering with Atsena Therapeutics to advance ATSN-101, an investigational #GeneTherapy aiming to restore vision.

Learn more: https://ow.ly/GCzY50XpZ2s

#LCA1 #RareDisease https://x.com/NSPharmaInc/status/1988623324562268474/photo/1

nspharmainc NS Pharma @nspharmainc ·
10 Nov

🌟 Welcome Susan Wierzbicki to our #QualityAssurance team as a Senior Auditor! 👏

With 20+ years in GCP audit management, compliance & vendor qualification, most recently at TKL Research, she brings deep expertise to #NSPharma. We’re thrilled to have you, Susan! 💙 https://x.com/NSPharmaInc/status/1987898435870032358/photo/1

nspharmainc NS Pharma @nspharmainc ·
7 Nov

We’re excited to join #CureDuchenne for a special community dinner in Chicago! 💙

This is a night for caregivers & families impacted by Duchenne and Becker to connect & find support together.

🗓️ Nov 8, 6–9 PM
📍 Chicago Prime Steakhouse.

RSVP: https://ow.ly/CJPY50XnBRz https://x.com/NSPharmaInc/status/1986811620069191923/photo/1

nspharmainc NS Pharma @nspharmainc ·
6 Nov

A huge thank you to everyone who visited our poster at #AANEM2025 and to MaraWood, Michelle Previtera & Denise Quigley for sharing their insights! 💙

Did you miss us? View the poster here: https://ow.ly/fiui50XnBKc

#Duchenne #RareDiseases #ExonSkipping https://x.com/NSPharmaInc/status/1986449197164314827/photo/1

nspharmainc NS Pharma @nspharmainc ·
5 Nov

🏔️ We’re proud to sponsor #HopeForGus and their #EverestToEndDuchenne trek!

This inspiring journey to the Everest Base Camp raises awareness & funds for DMD research, with each step symbolizing hope & determination. 💙

Learn more: https://everesttoendduchenne.org

#NSPharma https://x.com/NSPharmaInc/status/1986086846653235408/photo/1

nspharmainc NS Pharma @nspharmainc ·
3 Nov

Please join us in welcoming Marcel Bourgeois to #NSPharma as National Director!

With 15+ years in #PatientAccess, including leadership at Takeda, he’s launched programs & teams improving access for rare disease patients. Excited to have you aboard!

#NewHire https://x.com/NSPharmaInc/status/1985361947546534020/photo/1

nspharmainc NS Pharma @nspharmainc ·
31 Oct

We are conducting a Phase 2 #ClinicalTrial evaluating NS-229, an investigational JAK1 inhibitor, to learn more about potential new treatment options for adults with #EGPA.

See if you are eligible to join:
https://clinicaltrials.gov/study/NCT06046222#participation-criteria

#PatientRecruitment #NSPharma https://x.com/NSPharmaInc/status/1984260117773115792/photo/1