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Welcome Audra Lapati to #NSPharma as Area Business Manager!

With 20+ years in strategic account management across neurology, oncology & rare diseases, including roles at UCB, Takeda & Nutricia, she brings deep expertise to our team. We’re thrilled to have you!

#NewHire https://x.com/NSPharmaInc/status/1990435367749644518/photo/1

We’re excited to attend the #CureDuchenne Workshop in Boston!

This event unites families, clinicians & researchers to improve outcomes for those living with Duchenne.

πŸ“… November 15
πŸ•˜ 8:00 AM – 4:00 PM
πŸ“The Westin Waltham

Learn more & register: https://ow.ly/kjq750XpZkL https://x.com/NSPharmaInc/status/1989348045683560634/photo/1

Leber congenital amaurosis is caused by mutations in the GUCY2D gene, disrupting retinal function.

We're partnering with Atsena Therapeutics to advance ATSN-101, an investigational #GeneTherapy aiming to restore vision.

Learn more: https://ow.ly/GCzY50XpZ2s

#LCA1 #RareDisease https://x.com/NSPharmaInc/status/1988623324562268474/photo/1

🌟 Welcome Susan Wierzbicki to our #QualityAssurance team as a Senior Auditor! πŸ‘

With 20+ years in GCP audit management, compliance & vendor qualification, most recently at TKL Research, she brings deep expertise to #NSPharma. We’re thrilled to have you, Susan! πŸ’™ https://x.com/NSPharmaInc/status/1987898435870032358/photo/1

We’re excited to join #CureDuchenne for a special community dinner in Chicago! πŸ’™

This is a night for caregivers & families impacted by Duchenne and Becker to connect & find support together.

πŸ—“οΈ Nov 8, 6–9 PM
πŸ“ Chicago Prime Steakhouse.

RSVP: https://ow.ly/CJPY50XnBRz https://x.com/NSPharmaInc/status/1986811620069191923/photo/1

A huge thank you to everyone who visited our poster at #AANEM2025 and to MaraWood, Michelle Previtera & Denise Quigley for sharing their insights! πŸ’™

Did you miss us? View the poster here: https://ow.ly/fiui50XnBKc

#Duchenne #RareDiseases #ExonSkipping https://x.com/NSPharmaInc/status/1986449197164314827/photo/1

πŸ”οΈ We’re proud to sponsor #HopeForGus and their #EverestToEndDuchenne trek!

This inspiring journey to the Everest Base Camp raises awareness & funds for DMD research, with each step symbolizing hope & determination. πŸ’™

Learn more: https://everesttoendduchenne.org

#NSPharma https://x.com/NSPharmaInc/status/1986086846653235408/photo/1