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nspharmainc NS Pharma @nspharmainc ·
4h

We’re looking forward to attending the #AkariFoundation Workshop on March 14 to 15, 2026!

These gatherings create space for meaningful dialogue, shared learning and continued progress in rare disease research and care.

Learn more: https://ow.ly/rRwc50YsKu9

#CommunityEngagement https://x.com/NSPharmaInc/status/2032110025502490713/photo/1

nspharmainc NS Pharma @nspharmainc ·
11 Mar

We’re attending the Project Alive Building a Future Together Conference on March 14–15, 2026!

We're excited to connect and engage with families in the Hunter syndrome community.

Learn more: https://ow.ly/osHN50Ysg0F

#ProjectAlive #HunterSyndrome #MPSII #RareDiseases #NSPharma https://x.com/NSPharmaInc/status/2031747516929044545/photo/1

nspharmainc NS Pharma @nspharmainc ·
10 Mar

We’re presenting new 4.5-year data for brogidirsen (NS-089/NCNP-02), an investigational exon 44 skipping therapy for #Duchenne muscular dystrophy.

Results showed maintenance of motor function with no serious or severe adverse events reported.

Read more: https://ow.ly/bwnk50YrGON https://x.com/NSPharmaInc/status/2031385094066192565/photo/1

nspharmainc NS Pharma @nspharmainc ·
9 Mar

Our team is onsite at MDA 2026 and looking forward to engaging with our community! On Sunday and Monday, we’ll be presenting three additional posters highlighting real world evidence. Stop by posters 146 M, 168 M & 57 S to learn more! https://x.com/NSPharmaInc/status/2031022786383147476/photo/1

nspharmainc NS Pharma @nspharmainc ·
6 Mar

Please welcome Cassandra Kaufhold to NS Pharma as a Medical Science Liaison!

With 7+ years of translational research in neurodegenerative and rare diseases and a PhD in Neuroscience, Cassandra brings deep scientific expertise to our Medical Affairs team.

#NewHire #NSPharma https://x.com/NSPharmaInc/status/2029935438018814089/photo/1

nspharmainc NS Pharma @nspharmainc ·
4 Mar

Looking for support? You’re not alone.

The Little Hercules Foundation offers a searchable tool to find local housing, food and financial resources by ZIP code for families navigating #RareDiseases.

Learn more: https://ow.ly/t5KP50YoYU7

#LittleHercules #NSPharma https://x.com/NSPharmaInc/status/2029210642431848678/photo/1

nspharmainc NS Pharma @nspharmainc ·
2 Mar

We’re headed to Orlando for the 2026 MDA Clinical & Scientific Conference, presenting five abstracts including long term data from an open label extension study of brogidirsen (NS-089/NCNP-02) for #DMD amenable to exon 44 skipping.

Visit us at booth 213!

#NSPharma https://x.com/NSPharmaInc/status/2028485856261009458/photo/1