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FDA Accepts Biologics License Application for Duchenne Muscular Dystrophy Cardiomyopathy Treatment

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nspharmainc NS Pharma @nspharmainc ·
24 Mar

Duchenne is part of the story, not the whole story.

Brantley was diagnosed with DMD at 4. #ExonSkipping therapies can help produce a usable form of dystrophin, slowing progression so patients can keep pursuing what they love.

Learn more: https://ow.ly/tLgj50Yy39p https://x.com/NSPharmaInc/status/2036458150723768404/video/1

nspharmainc NS Pharma @nspharmainc ·
20 Mar

We’re proud to support the 2026 Brian McKenna #TetraSki Express National Championship on March 27 in Utah!

This inspiring event showcases adaptive technology, resilience and athleticism in downhill racing.

Learn more: http://www.tetraski.us/tetraski-express

#AdaptiveSports #NSPharma https://x.com/NSPharmaInc/status/2034993922947063856/photo/1

nspharmainc NS Pharma @nspharmainc ·
18 Mar

We’re glad to be part of this upcoming #CureDuchenne event!

These moments help us reflect, connect and stay focused on improving care and access. We look forward to seeing you there.

Learn more: https://web.cvent.com/event/a4ee9964-3748-4016-b032-1b4c3b2df2f0/summary

#NSPharma https://x.com/NSPharmaInc/status/2034284219602489364/photo/1

nspharmainc NS Pharma @nspharmainc ·
16 Mar

Thanks to #Project Alive and the #HunterSyndrome community for a meaningful Building a Future Together Conference!

It was inspiring to connect with families, advocates and leaders in Costa Mesa and share conversations that help advance rare disease care and research.

#NSPharma https://x.com/NSPharmaInc/status/2033559440838852717/photo/1

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nspharmainc NS Pharma @nspharmainc ·
13 Mar

That’s a wrap on MDA 2026! If you missed our presentations, you can view them here:

• https://ow.ly/SVRx50Yth37
• https://ow.ly/bjGZ50Yth35
• https://ow.ly/mZ7n50Yth38
• https://ow.ly/uVmT50Yth36

#MDAConference #Duchenne #ClinicalResearch #NSPharma https://x.com/NSPharmaInc/status/2032457121791353114/photo/1

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nspharmainc NS Pharma @nspharmainc ·
12 Mar

We’re looking forward to attending the #AkariFoundation Workshop on March 14 to 15, 2026!

These gatherings create space for meaningful dialogue, shared learning and continued progress in rare disease research and care.

Learn more: https://ow.ly/rRwc50YsKu9

#CommunityEngagement https://x.com/NSPharmaInc/status/2032110025502490713/photo/1

nspharmainc NS Pharma @nspharmainc ·
11 Mar

We’re attending the Project Alive Building a Future Together Conference on March 14–15, 2026!

We're excited to connect and engage with families in the Hunter syndrome community.

Learn more: https://ow.ly/osHN50Ysg0F

#ProjectAlive #HunterSyndrome #MPSII #RareDiseases #NSPharma https://x.com/NSPharmaInc/status/2031747516929044545/photo/1