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FDA Accepts Biologics License Application for Duchenne Muscular Dystrophy Cardiomyopathy Treatment

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Please join us in welcoming Marcel Bourgeois to #NSPharma as National Director!

With 15+ years in #PatientAccess, including leadership at Takeda, he’s launched programs & teams improving access for rare disease patients. Excited to have you aboard!

#NewHire https://x.com/NSPharmaInc/status/1985361947546534020/photo/1

We are conducting a Phase 2 #ClinicalTrial evaluating NS-229, an investigational JAK1 inhibitor, to learn more about potential new treatment options for adults with #EGPA.

See if you are eligible to join:
https://clinicaltrials.gov/study/NCT06046222#participation-criteria

#PatientRecruitment #NSPharma https://x.com/NSPharmaInc/status/1984260117773115792/photo/1

We’re proud to sponsor the Jett Foundation’s final 2025 Family Workshop in Norfolk, VA!

Join us on Saturday Nov 8 for a day of learning, connection & empowerment supporting the Duchenne community.

Register here: https://ow.ly/gSuH50Xif1a

#Duchenne #NSPharma #CommunitySupport https://x.com/NSPharmaInc/status/1983534797260575194/photo/1

🌟 Welcome Shannon Merkel to NS Pharma as our new Director of #MarketAccess Marketing Communications!

With 20+ years in market access, payer policy & launch excellence - including a decade at Takeda - she brings deep expertise & passion to our team. 💙

#NewHire #NSPharma https://x.com/NSPharmaInc/status/1983172404311425345/photo/1

Excited to share new data at #AANEMinSanFran!

Don’t miss our poster on exon-skipping therapy persistence:

Thu 10/30 - 6:15 PM
Fri 10/31 - 2:45 PM.

Join Mara Wood & Denise Quigley to discuss insights for the #Duchenne community. See you in San Francisco! 💙

#RareDiseases https://x.com/NSPharmaInc/status/1982810230544023727/photo/1

We’re excited to attend the 10th Annual #UPINFamilyDay Conference on Oct 25 at the Loveland Living Planet Aquarium! 🐠

A day of learning, connection & fun for families impacted by neuromuscular disorders.

Register to join us: https://ow.ly/fAV150XgP4w

#RareDiseases #NSPharma https://x.com/NSPharmaInc/status/1981722931592937623/photo/1

At #NSPharma, we’re committed to advancing science & hope for #RareDiseases.

This #HunterSyndromeAwareness Week (Oct 19–25), we stand with families & advocates to raise awareness of #MPSII, a rare genetic disorder that primarily affects boys.

Learn more: https://ow.ly/1Wna50XgOW1 https://x.com/NSPharmaInc/status/1981360732408013020/photo/1