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nspharmainc NS Pharma @nspharmainc ·
16 Feb

Please welcome Saori Yamaguchi to #NSPharma as Associate Director, Business Development.

With 10+ years of global experience across pharma and consulting, Saori brings strong expertise in strategy and launch planning. We’re excited to have her on the team!

#NewHire https://x.com/NSPharmaInc/status/2023412550486860231/photo/1

nspharmainc NS Pharma @nspharmainc ·
13 Feb

What an incredible experience at #WORLDSymposium 2026. We were grateful to welcome over 70 attendees to our #MPSII session.

Thank you to Drs. Hoffman, Burton and Jalazo for an outstanding discussion and to everyone who joined, asked questions, and helped make it so impactful. https://x.com/NSPharmaInc/status/2022325330032161027/photo/1

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nspharmainc NS Pharma @nspharmainc ·
11 Feb

Today we celebrate #InternationalDayofWomenandGirlsinScience by recognizing the women at #NSPharma whose leadership and dedication drive progress.

Across research, development and patient focused roles, their expertise strengthens innovation and advances #RareDisease care. https://x.com/NSPharmaInc/status/2021600138397933684/video/1

nspharmainc NS Pharma @nspharmainc ·
9 Feb

We’re Hiring a #PatientEngagement Lead to support individuals and families living with #RareDiseases.

You could help patients navigate access, support, and care for conditions like #Duchenne and Hunter syndrome.

Learn more and apply: https://ow.ly/4wIE50Yby0l

#NSPharma https://x.com/NSPharmaInc/status/2020877306554634374/photo/1

nspharmainc NS Pharma @nspharmainc ·
6 Feb

We’re looking forward to attending #CureDuchenne Atlanta!

These sessions support meaningful dialogue and collaboration among patients, caregivers, healthcare professionals, and researchers.

Learn more here: https://ow.ly/QVMT50Y9Qz4

#NSPharma #RareDiseases #CommunityEngagement https://x.com/NSPharmaInc/status/2019788549822841016/photo/1

nspharmainc NS Pharma @nspharmainc ·
4 Feb

What if treatment could go beyond managing symptoms?

#NSPharma is exploring #GeneTherapy as an evolving area of research to treat certain genetic conditions at the genetic level.

Learn more about Gene Therapy here: https://ow.ly/f5tP50Y8GO3

#RareDiseases #PatientEducation https://x.com/NSPharmaInc/status/2019063422738952334/video/1

nspharmainc NS Pharma @nspharmainc ·
2 Feb

We’re proud to be presenting at #WORLDSymposium 2026 today. This meeting brings together the lysosomal disease community to share knowledge, foster collaboration, and advance #RareDisease research.

#NSPharma is honored to contribute and connect with others committed to progress. https://x.com/NSPharmaInc/status/2018338969201578443/photo/1