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nspharmainc NS Pharma @nspharmainc ·
7 Oct

We're in Austria for #WMS2025!

Don't miss the poster presentation (658P) by the National Center of Neurology and Psychiatry (NCNP) in the exhibit hall on October 8.

We look forward to sharing this our latest data with the community and hope to see you there!

#GeneTherapy https://x.com/NSPharmaInc/status/1975562483998794142/photo/1

nspharmainc NS Pharma @nspharmainc ·
3 Oct

Adults living with eosinophilic granulomatosis with polyangiitis (#EGPA) could take part in a Phase 2 clinical trial of NS-229, an investigational JAK1 inhibitor.

Learn more and explore participation: https://ow.ly/nm9w50X65UE

#ClinicalTrial #RareDisease #PatientRecruitment #EGPA https://x.com/NSPharmaInc/status/1974112964614443109/photo/1

nspharmainc NS Pharma @nspharmainc ·
2 Oct

When should we start therapy to increase our child’s dystrophin?🔍

Starting early can help slow the progression of #Duchenne but it can be effective at any age, even years after diagnosis!

Learn more: https://ow.ly/Fcig50X4W4y

#DuchenneAwareness #Dystrophin #ExonSkipping https://x.com/NSPharmaInc/status/1973733488345206800/photo/1

nspharmainc NS Pharma @nspharmainc ·
1 Oct

This year’s Kindness Over Muscular Dystrophy Annual Benefit was nothing short of inspiring!

From local bites and brews to exciting auctions and raffles, the energy in the room was matched only by the generosity of those supporting the Duchenne and Becker community. ✨

#KOMD2025 https://x.com/NSPharmaInc/status/1973409260420632966/photo/1

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nspharmainc NS Pharma @nspharmainc ·
29 Sep

Join us in Ontario this Saturday (10/4) for Project Alive’s Hunter Syndrome Friends & Family Gathering! 🎉

Celebrate San Bernardino’s recognition of October’s 3rd week as Hunter Syndrome Awareness Week 💜

RSVP: https://ow.ly/rHer50X3KHN

#HunterSyndrome #MPSII https://x.com/NSPharmaInc/status/1972688585284268379/photo/1

nspharmainc NS Pharma @nspharmainc ·
26 Sep

We’re excited to be in Salt Lake City with our friends from @CureDuchenne for a special community dinner!

This evening is a wonderful chance to connect, share experiences, and find support together.

Reserve your spot: https://ow.ly/w83E50X0J8E

#CureDuchenne #CureDuchenneCares https://x.com/NSPharmaInc/status/1971575492407955661/photo/1

nspharmainc NS Pharma @nspharmainc ·
25 Sep

Say hello to Lori Amels, one of our new Key Account Managers on the Commercial Sales team!

With a strong background across gene therapy, ophthalmology and neurology, Lori’s expertise is matched by her passion for helping patients and families.

#Welcome to NS Pharma!

#NewHire https://x.com/NSPharmaInc/status/1971213265150652772/photo/1