NS Pharma is working to have an important impact on the lives of patients with rare diseases. Our therapeutic areas encompass neurological diseases and inflammatory diseases.
Harnessing the power of innovative science can help bring new treatments to patients with rare diseases. NS Pharma is developing therapies through exon-skipping, cell therapy and JAK1 inhibition technology.
NS Pharma is working to have an important impact on the lives of patients with rare diseases. Our therapeutic areas encompass neurological diseases and inflammatory diseases.
Harnessing the power of innovative science can help bring new treatments to patients with rare diseases. NS Pharma is developing therapies through exon-skipping, cell therapy and JAK1 inhibition technology.
Press Release / July 1, 2025
NS Pharma Announces Strategic Alliance with Boston Children’s Hospital to Develop New Therapies for Rare Diseases
Happy International Youth Day!
Today, we’re celebrating the incredible young people who inspire us every single day, especially our amazing ambassadors.
Ensuring their futures are as bright as possible fuels our purpose!
#InternationalYouthDay #DuchenneAwareness #RareDisease https://x.com/NSPharmaInc/status/1955268572659282123/photo/1
We had a great time at the #MPSSociety Family Conference last week!
A big thank you to the @MPSSociety for hosting such a powerful and uplifting event. And shout-out to @REGENXBIO and Adam Gold for sharing exciting updates on our partnership!
#MPSFamily2025 #MPS #RareDiseases https://x.com/NSPharmaInc/status/1954905648971591952/photo/1
Heading to Orlando this weekend? So are we, and we’d love to see you there! 💙
Join us for another fantastic @CureDuchenne Neighborhood Dinner. Let's come together, share stories and find support in one another.
Register here: https://ow.ly/1U2c50WztoH
#CureDuchenneCares #DMD https://x.com/NSPharmaInc/status/1953818490206662678/photo/1
The @MPSSociety Family Conference kicks off tomorrow and we’re thrilled to be part of it! 🎉
Be sure to catch REGENXBIO's presentation at 12:15pm for some exciting updates on our partnership!
Register here: https://ow.ly/E8i250Wzoeq
#MPSSociety #MPSAwareness #MPSFamily2025 https://x.com/NSPharmaInc/status/1953093710268494006/photo/1
We’re thrilled to be sponsoring the Akari Foundation #FamilyFestival this weekend! ☀️
This event brings together families affected by #Duchenne and other #NeuromuscularConditions for a day full of connection, community and support.
Register here: https://ow.ly/WxiR50WznZP https://x.com/NSPharmaInc/status/1952369589460828510/photo/1
At NS Pharma, we’re working hard to advance treatments for #EGPA with our selective JAK1 inhibitor, NS‑229.
Did you know that we’ve been granted #OrphanDrugDesignation in the EU & US, and are now in a global Phase II trial? 🌟
Learn more: https://ow.ly/zUzm50WxirA
#RareDisease https://x.com/NSPharmaInc/status/1951282216492732596/photo/1
Last week, we spent a magical day in the Colorado Rockies at #CampPromise Denver! ⛺
Big thanks to the @JettFoundation for creating such a welcoming space for everyone involved. We’ll definitely be back again next year!
#DuchenneCommunity #RareDisease https://x.com/NSPharmaInc/status/1950557000435171827/photo/1
