Building healthier futures powered by thoughtful science

We are a highly focused, research-driven biopharmaceutical company working in rare diseases. We're exploring the potential of cutting-edge science as a subsidiary of Nippon Shinyaku Co., Ltd. In Japan.

Advancing rare disease research

Inspired by our own families, as well as the individuals we aim to provide with treatment, NS Pharma is conducting advanced research in rare diseases, including exon-skipping technology, to offer new, effective treatment options for Duchenne. We’re also developing JAK1 inhibition for the potential treatment of eosinophilic granulomatosis with polyangiitis (EGPA).

Therapeutic areas

NS Pharma is working to have an important impact on the lives of patients with rare diseases. Our therapeutic areas encompass neurological diseases and inflammatory diseases.

Scientific approaches

Harnessing the power of innovative science can help bring new treatments to patients with rare diseases. NS Pharma is developing therapies through exon-skipping, cell therapy and JAK1 inhibition technology.

Therapeutic areas

NS Pharma is working to have an important impact on the lives of patients with rare diseases. Our therapeutic areas encompass neurological diseases and inflammatory diseases.

Scientific approaches

Harnessing the power of innovative science can help bring new treatments to patients with rare diseases. NS Pharma is developing therapies through exon-skipping, cell therapy and JAK1 inhibition technology.

From our blog

Press Release / October 14, 2025

Brogidirsen (NS-089/NCNP-02) 3.5 Year Clinical Trial Data for the Treatment of Duchenne Muscular Dystrophy Presented at 2025 World Muscle Society Congress

Press Release / September 19, 2025

FDA Grants Orphan Drug Designation to NS-051/NCNP-04 for the Treatment of Duchenne Muscular Dystrophy

Press Release / September 9, 2025

FDA Grants Fast Track Designation to NS-229 for the Treatment of Eosinophilic Granulomatosis with Polyangiitis

Press Release / October 14, 2025

Brogidirsen (NS-089/NCNP-02) 3.5 Year Clinical Trial Data for the Treatment of Duchenne Muscular Dystrophy Presented at 2025 World Muscle Society Congress

Press Release / September 19, 2025

FDA Grants Orphan Drug Designation to NS-051/NCNP-04 for the Treatment of Duchenne Muscular Dystrophy

Press Release / September 9, 2025

FDA Grants Fast Track Designation to NS-229 for the Treatment of Eosinophilic Granulomatosis with Polyangiitis

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Social media

We’re looking forward to #WORLDSymposium 2026, where the global lysosomal disease community comes together to share science and progress.

#NSPharma is proud to present and engage with everyone working to advance care for #RareDiseases.

Register here: https://ow.ly/JFCf50Y3CxG https://x.com/NSPharmaInc/status/2015802240548708807/photo/1

Please welcome Shaun Flaherty to #NSPharma as Area Business Director!

With 15+ years in sales leadership, account management and reimbursement across oncology, urology and cardiology, Shaun brings deep experience to the team. We're excited to have you on board!

#NewHire https://x.com/NSPharmaInc/status/2014715146149491166/photo/1

#NSPharma is proud to sponsor #ClinicalTrials for brogidirsen (NS-089/NCNP-02), which has 3.5-year efficacy and safety data presented at the 2025 World Muscle Society Congress.

Learn more about #DMD clinical trials: https://ow.ly/xkFf50Y0xOf https://x.com/NSPharmaInc/status/2013990329590992938/photo/1

NSPharma is proud to sponsor #PPMD Understanding Dystrophinopathy Care event in New York, Jan 21–23.

This gathering brings us together to connect, and share our insights and experiences in #Duchenne and #Becker care.

Learn more & register: https://donate.parentprojectmd.org/event/understanding-dystrophinopathy-care-in-an-evolving-environment/e718213

#RareDisease https://x.com/NSPharmaInc/status/2013265639020933504/photo/1

#WelcomeToTheTeam Jared Sternberg as HCP Marketing Senior Manager!

With 20+ years of experience across CNS, neurology, endocrinology and rare diseases, Jared brings deep launch and strategy expertise from Amneal, Allergan, and more. #NSPharma is excited to have you!

#NewHire https://x.com/NSPharmaInc/status/2012178431190958491/photo/1

We’re excited to join families, caregivers, clinicians and researchers for a day of learning and connection at the latest #CureDuchenne Workshop!

📅 Jan 17, 8 AM–4 PM
📍 Miami Marriott Dadeland.

Register here: https://ow.ly/5Wr950XWByg

#RareDisease #NSPharma https://x.com/NSPharmaInc/status/2011453701387411636/photo/1

We’re continuing to grow our team at #NSPharma. We’re #NowHiring a Senior Director, Market Access, a key role for an experienced leader passionate about improving access to therapies for people living with #RareDiseases.

Learn more and apply: https://ow.ly/E25F50XVpZ6 https://x.com/NSPharmaInc/status/2010728774531256724/photo/1