NS Pharma is working to have an important impact on the lives of patients with rare diseases. Our therapeutic areas encompass neurological diseases and inflammatory diseases.
Harnessing the power of innovative science can help bring new treatments to patients with rare diseases. NS Pharma is developing therapies through exon-skipping, cell therapy and JAK1 inhibition technology.
NS Pharma is working to have an important impact on the lives of patients with rare diseases. Our therapeutic areas encompass neurological diseases and inflammatory diseases.
Harnessing the power of innovative science can help bring new treatments to patients with rare diseases. NS Pharma is developing therapies through exon-skipping, cell therapy and JAK1 inhibition technology.
Press Release / May 14, 2025
FDA Accepts Biologics License Application for Mucopolysaccharidosis II Treatment
The JettFoundation #NationalChallenge is a wrap—and we’re so proud to have been part of it.
Together, we’ve logged over 15k steps!
A HUGE thanks to everyone who took part and to the Jett Foundation for leading the charge!🙌
#TeamJett #DuchenneAwareness https://x.com/NSPharmaInc/status/1932075215342756203/photo/1
This June, we’re putting purpose into motion! 💪
Victoria Ramirez, our amazing Clinical Research Manager is leading the #RelayForLife in Paramus & we couldn’t be prouder.
Let’s show team Victorious some love & support!
Donate here: https://ow.ly/amHv50W48Xt
#CancerSurvivorMonth https://x.com/NSPharmaInc/status/1930988556559790380/photo/1
Did you know, #ExonSkipping helps the body bypass a #GeneticMutation to produce #Dystrophin that’s 84–97% as long as usual.
Whereas, #GeneTherapy inserts an engineered micro-dystrophin gene, creating a protein that’s 32–40% as long.
Learn more: https://ow.ly/LzuM50W2qIh https://x.com/NSPharmaInc/status/1930263647038603288/photo/1
The @JettFoundation #NationalChallenge officially kicked off yesterday and Team NS Pharma is proud to sponsor this critical event!
Doesn't our team look fabulous in their Jett Foundation t-shirts?
How are you going to move for #TeamJett?! 💙
#DuchenneAwareness #RareDisease https://x.com/NSPharmaInc/status/1929538498320621624/photo/1
Ahead of #NationalSmileDay tomorrow, we’re celebrating the positivity that shines so brightly across the #Duchenne community.
We asked our amazing ambassadors, “What makes you smile?” - and their answers warmed our hearts. 💛
#RareDiseases #DMD https://x.com/NSPharmaInc/status/1928451465128915286/video/1
Some moments speak louder than words 💙
It’s bonds like these that inspire us every day to keep pushing forward - for better care, more research and a future full of hope for the Duchenne community!
#Duchenne #FUTURES2025 #CureDuchenne #TogetherForDuchenne https://x.com/NSPharmaInc/status/1928089486526742678/photo/1
What an incredible few days at #FUTURES2025! 💙
It was a pleasure connecting with so many incredible people, all united by a shared commitment to improving the lives of the #DuchenneCommunity.
A big thanks to @CureDuchenne for hosting such an impactful event!
#CureDuchenne https://x.com/NSPharmaInc/status/1927726563682074796/photo/1
